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Disease Reportsspinal muscular atrophy
MeSH D009134 - spinal muscular atrophy
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D013118:Spinal cord diseases
0 Companies
0 Drugs
Success rate
D016472:Motor neuron disease
0 Companies
0 Drugs
Success rate
D009134: 
Spinal muscular atrophy
$
Success rate
D014897:Spinal muscular atrophies of childhood
0 Companies
0 Drugs
Success rate
D055534:X-linked bulbo-spinal atrophy
0 Companies
0 Drugs
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
BiogenNusinersen Spinraza  2017-05-30 $1,639.2 M Q2/23-Q1/24 
NovartisOnasemnogene abeparvovec Zolgensma  2019-05-24 $1,210 M Q2/20-Q2/23 
RocheRisdiplam Evrysdi  2021-03-26 $1,623.688 M Q4/22-Q3/23 
Clinical Trials
Historical Success Rate
Phase 1
69%
9/13
Phase 2
36%
9/25
Phase 3
53%
8/15
Approved: 5Overall Success rate: 13%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
Biogen
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